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Review
. 2018 Oct;39(5):560-568.
doi: 10.1080/13816810.2018.1495745. Epub 2018 Jul 24.

VSports最新版本 - Gene therapy in inherited retinal degenerative diseases, a review

Vitor K L Takahashi  1   2   3 , Júlia T Takiuti  1   2   4 , Ruben Jauregui  1   2   5 , Stephen H Tsang  1   2   6
Affiliations
Review

Gene therapy in inherited retinal degenerative diseases, a review

Vitor K L Takahashi et al. Ophthalmic Genet. 2018 Oct.

Abstract

Hereditary diseases of the retina represent a group of diseases with several heterogeneous mutations that have the common end result of progressive photoreceptor death leading to blindness VSports手机版. Retinal degenerations encompass multifactorial diseases such as age-related macular degeneration, Leber congenital amaurosis, Stargardt disease, and retinitis pigmentosa. Although there is currently no cure for degenerative retinal diseases, ophthalmology has been at the forefront of the development of gene therapy, which offers hope for the treatment of these conditions. This article will explore an overview of the clinical trials of gene supplementation therapy for retinal diseases that are underway or planned for the near future. .

Keywords: Adeno-associated virus; gene therapy; inherited retinal diseases. V体育安卓版.

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